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Adeno-associated viral vector-mediated gene transfer results in long-term enzymatic and functional correction in multiple organs of Fabry mice

  • Sung Chul Jung
  • , Ina P. Han
  • , Advait Limaye
  • , Ruian Xu
  • , Monique P. Gelderman
  • , Patricia Zerfas
  • , Kamala Tirumalai
  • , Gary J. Murray
  • , Matthew J. During
  • , Roscoe O. Brady
  • , Pankaj Qasba

Research output: Contribution to journalArticlepeer-review

145 Scopus citations

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